MOOC on gene and gene-based cell therapies for rare diseases
Foundation For Rare Diseases (Fondation Maladies Rares, France) organises an online MOOC on gene and gene-based cell therapies for rare diseases . The course features contributions from leading U.S. and European researchers — including Alain Fischer, Heather Gray Edwards, Alessio Cantore, Zoltan Ivics, Sylvie Odent, Salima Hacein-Bey-Abina, Manuel Gonçalves, Marina Cavazzana, Allison Bradbury, Anne Galy, Chantal Pichon, Claire Booth, Jeffrey Medin , among others — as well a
FDA approval of LAD gene therapy
Last Thursday, the FDA approved the LAD gene therapy developed by Juan A. Bueren and Elena Almarza, in collaboration with the Adrian Thrasher team. This treatment was licensed to Rocket Pharma, who developed the clinical trial and presented it to the FDA. We believe this is terrific news for the gene therapy field and for SETGYC, as a lot of these advances have come from SETGYC members, and the society has played a fundamental role in favouring this collaboration and in the d
En memoria del Dr Ernest Arenas Cases (1962 – 2024)
El “Professor” Ernest Arenas nos ha dejado de forma prematura e inesperada. Brillante neurocientífico y excelente persona. Una vida dedicada a la ciencia, abordando uno de los principales retos médicos de nuestra sociedad: la búsqueda de tratamientos para las enfermedades neurodegenerativas. El Dr Arenas nació en 1962 en Lleida, aunque pasó su infancia en Manresa. Estudió Medicina y Cirugía en la Universidad de Lleida. Posteriormente realizó su tesis doctoral en la Universida
